Researchers have developed a gene-editing treatment for prion disease that extends lifespan by about 50 percent in a mouse model of the fatal neurodegenerative condition. The treatment, which uses ...

An approach that specifically targets a single nucleotide corrected behavioural abnormalities in an animal model of Snijders Blok–Campeau syndrome. Snijders Blok–Campeau syndrome, which is associated ...

A research team has successfully demonstrated the world's first gene-editing treatment for Leber's hereditary optic neuropathy (LHON). The study was conducted in collaboration with the Seoul National ...

CRISPR has taken the bioengineering world by storm since its first introduction. From treating sickle cell diseases to creating disease-resistant crops, the technology continues to boast success on ...

ARPA-H gene editing program THRIVE awards $160 million to seven research teams tasked with building scalable base-editing ...

C RISPR-Cas9 technology has revolutionized biology, largely because of its simplicity compared to previous gene editing techniques. However, it still takes weeks to learn, design, perform, and analyze ...

Gene editing has delivered remarkable results against sickle cell disease. Now researchers are working to make these ...

Imagine a future where treating cystic fibrosis is as simple as taking a deep breath. That’s exactly what a team of pediatric physician-scientists at the Eli and Edythe Broad Center of Regenerative ...

"Traditional gene-editing technologies work best with single mutations and are expensive to optimize, so gene therapies tend to focus on the mutations that are the most common," Buffington said. "But ...

Revolutions in gene therapy are rapidly changing the landscape of modern medicine. Revolutions in gene therapy are rapidly changing the landscape of modern medicine, forcing society and science alike ...

New research shows it’s possible to edit the DNA of human embryos with more precision. But scientists warn it’s still not ...